Bridging Gaps, Optimizing Treatment in Patients With LC-FAODs copertina

Bridging Gaps, Optimizing Treatment in Patients With LC-FAODs

Bridging Gaps, Optimizing Treatment in Patients With LC-FAODs

Di: Annenberg Center for Health Sciences
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A proposito di questo titolo

Patients with long-chain fatty oxidation disorders (LC-FAODs) have historically been treated with diet modification and even-carbon medium-chain triglyceride (MCT) supplementation. In this 45-minute, case-based, modular activity, Sandra van Calcar, PhD, RD, LD, and Jerry Vockley, MD, PhD, address key topics, including disease presentation, historical treatment, emerging treatment with triheptanoin, and nutritional planning specific to patients with LC-FAODs.Annenberg Center for Health Sciences Disturbo fisico e malattia Igiene e vita sana
  • Clinical Case Vignettes
    Nov 14 2024
    • Initiating triheptanoin
    • Dosing modification to improve tolerability
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    10 min
  • Optimizing Triheptanoin Therapy
    Nov 14 2024
    • Clinical safety and efficacy
    • Initiation and titration
    • Administration considerations
    • Individualizing treatment
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    19 min
  • Historical Treatment; Introduction of Triheptanoin
    Nov 14 2024
    • Dietary modification
    • MCT supplementation
    • Triheptanoin mechanism of action
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    6 min
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